Genetics
Genetics
More in Genetics
Phase III trial falls short of efficacy target, but positive signal emerges in younger kids
Aug 23, 2024
![A computer rendering of red blood cells](http://assets.medpagetoday.net/media/images/111xxx/111655.jpg)
This is the second time the drug has been submitted to the FDA for Niemann-Pick disease type C
Aug 01, 2024
![FDA ADCOMM arimoclomol over a computer rendering of a strand of DNA.](http://assets.medpagetoday.net/media/images/111xxx/111325.jpg)
Studies show 90% reduction in intravitreal treatment burden, durable effect on vision, anatomy
Jul 18, 2024
![ASRS over a photo of Stockholmsmässan Convention Center in Stockholm, Sweden.](http://assets.medpagetoday.net/media/images/111xxx/111137.jpg)
U.S. clinics market oligonucleotide therapy for a wide range of conditions, without much evidence
Jul 05, 2024
![A computer rendering of an oligonucleotide aptamer attacking a cancer cell.](http://assets.medpagetoday.net/media/images/110xxx/110966.jpg)
Phase II study found brigatinib exceeded historical control by shrinking 10% of targeted tumors
Jun 21, 2024
![A computer rendering of a meningioma.](http://assets.medpagetoday.net/media/images/110xxx/110772.jpg)